A disease or disorder is defined as rare when it affects less than 1 in 2000. One rare disease may affect only a handful of patients, and another as many as 5000 in Belgium alone. In total, more than 6000 rare diseases are known, and around 350 million people are affected by rare diseases worldwide. So, rare might not be so rare after all.
Nearly 50% of rare diseases begin in childhood and on average, getting the right diagnosis can take up to 5-7 years, requiring visits to eight different specialists.
Takeda is fully committed to fight against rare diseases, maximizing value from approved brands and advancing treatments in the pipeline across phase 1 to 3 and making them available for patients as fast as possible. The Rare Diseases Therapeutic Area Unit will focus initially on areas of expertise in haematology, immunology and lysosomal storage disorders (LSDs).