A disease or disorder is defined as rare when it affects less than 1 in 2000. In total, more than 6000 rare diseases are known, and around 400 million people are affected by rare diseases worldwide. In Belgium, more than 500 000 people suffer from a rare disease. Therefore, rare might not be so rare after all.
Nearly 50% of rare diseases begin in childhood and on average, getting the right diagnosis can take up to 5-7 years, requiring visits to as many as eight different specialists.
Takeda is fully committed to fight against rare diseases, advancing treatments in the pipeline across phase 1 to 3 and making them available for patients as fast as possible. The Rare Diseases Team focuses on areas of expertise in haematology, immunology and metabolic diseases.
https://globalgenes.org/rare-disease-facts/ Accessed January 24, 2022
https://www.everydayhealth.com/news/10-essential-facts-about-rare-diseases/ Accessed January 26, 2022